Mitochondrial Neurogastrointestinal Encephalopathy Syndrome - 6 Studies Found
Recruiting |
: MNGIE Allogeneic Hematopoietic Stem Cell Transplant Safety Study : Mitochondrial Neurogastrointestinal Encephalomyopathy (MNGIE) : 2015-02-10 : Biological: Hematopoietic Allogeneic Stem Cells HLA 10/10 matched allogeneic bone marrow cells will be i |
Recruiting |
: The Natural History Study of Mitochondrial NeuroGastroIntestinal Encephalopathy (MNGIE) : Mitochondrial NeuroGastroIntestinal Encephalopathy (MNGIE) : 2012-09-25 |
Enrolling by invitation |
: Tissue Sample Study for Mitochondrial Disorders :
: 2012-08-31 |
Recruiting |
: MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis :
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Completed |
: A Long-Term Extension Study of RP103-MITO-001 (NCT02023866) to Assess RP103 in Children With Inherited Mitochondrial Disease : Mitochondrial Diseases : 2015-06-10 : Drug: Cysteamine Bitartrate Delayed-release Capsules Treatment with experimental drug as detailed in arm |
Recruiting |
: North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC) :
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