Leigh Disease - 10 Studies Found
Completed |
: Safety and Efficacy Study of EPI-743 in Children With Leigh Syndrome : Leigh Syndrome : 2012-11-01 :
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Enrolling by invitation |
: Long-Term Safety and Efficacy Evaluation of EPI-743 in Children With Leigh Syndrome : Leigh Syndrome : 2014-08-21 : Drug: EPI-743 EPI-743 is a quinone oxidation product of alpha tocotrienol |
Recruiting |
: The Leigh Syndrome Registry :
: 2017-04-28 |
Completed |
: Open-Label, Dose-Escalating Study Assessing Safety, Tolerability, Efficacy, of RP103 in Mitochondrial Disease : Inherited Mitochondrial Disease, Including Leigh Syndrome : 2013-12-17 : Drug: Cysteamine Bitartrate Cysteamine Bitartrate Delayed-release Capsules |
Completed |
: A Dose-escalating Clinical Trial With KH176 :
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Enrolling by invitation |
: Tissue Sample Study for Mitochondrial Disorders :
: 2012-08-31 |
Recruiting |
: Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford :
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Active, not recruiting |
: EPI-743 for Mitochondrial Respiratory Chain Diseases : Mitochondrial Diseases : 2011-06-07 : Drug: EPI-743 EPI-743 is administered as a dose escalation from 50 mg bid to 100 mg tid |
Completed |
: A Long-Term Extension Study of RP103-MITO-001 (NCT02023866) to Assess RP103 in Children With Inherited Mitochondrial Disease : Mitochondrial Diseases : 2015-06-10 : Drug: Cysteamine Bitartrate Delayed-release Capsules Treatment with experimental drug as detailed in arm |
Recruiting |
: North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC) :
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