Aromatic L-amino Acid Decarboxylase Deficiency - 4 Studies Found
Completed |
: Newborn Screening for Aromatic L-amino Acid Decarboxylase Deficiency : Aromatic L-amino Acid Decarboxylase Deficiency : 2015-03-21 |
Recruiting |
: A Single-Stage, Adaptive, Open-label, Dose Escalation Safety and Efficacy Study of AADC Deficiency in Pediatric Patients : AADC Deficiency : 2016-07-20 : Drug: AAV2-hAADC Subjects will be enrolled sequentially in |
Recruiting |
: A Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC - An Expansion : Aromatic Amino Acid Decarboxylase Deficiency : 2016-10-03 : Drug: AAV2-hAADC Dosage form: Aqueous solutionDose(s): 2.371x1011 vg/case Dosing schedule: Intracerebral |
Completed |
: A Phase I/II Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC : Aromatic L-amino Acid Decarboxylase (AADC) Deficiency : 2011-06-12 : Drug: gene therapy AAV2-hAADC viral vector will be injected into bilateral putamen by stereotactic surge |