Metachromatic Leukodystrophy - 25 Studies Found
Recruiting |
: Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and Adrenoleukodystrophy :
: 2015-08-12 : Genetic: transduced CD34+ hematopoietic stem cell Autologous hematopoietic stem cells (HSCs) collected f |
No longer available |
: Allogeneic Stem Cell Transplantation for the Treatment of Multiple Sclerosis (Compassionate Use) : Metachromatic Leukodystrophy : 2014-03-07 : Biological: Enriched Hematopoetic Stem Cell Infusion Enriched Hematopoetic Stem Cell Infusion |
Recruiting |
: Biomarker for Metachromatic Leukodystrophy Disease :
: 2012-02-21 |
No longer available |
: Single Patient Expanded Access Protocol: Metabolic Boost : Metachromatic Leukodystrophy : 2013-12-19 : Biological: Enriched Hematopoetic Stem Cell Infusion Enriched Hematopoetic Stem Cell Infusion |
Active, not recruiting |
: Gene Therapy for Metachromatic Leukodystrophy : Lysosomal Storage Disease : 2012-03-16 : Genetic: Autologous CD34+ stem cells transduced with ARSA encoding lentiviral vector Autologous hematopo |
Terminated |
: Natural History Study of Children With Metachromatic Leukodystrophy :
|
Completed |
: Stem Cell Transplantation (SCT) for Genetic Diseases :
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Completed |
: Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoietic Stem Cell Transplantation :
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Completed |
: Stem Cell Transplant for Inborn Errors of Metabolism :
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